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ERS CONGRESS 2026 5-9 September | Barcelona , Spain First - in - human in vivo gene editing for severe alpha - 1 antitrypsin deficiency ( AATD ) : initial data from the Phase 1/2 study of BEAM - 302 John R Hurst , Emily FA van ' t Wout , Thomas Ashdown , Matthew Conron , N. Gerry McElvaney , Jeffrey Garrett , Ed Gane , Andrew A Wilson , Joe Kaserman , Charlie Strange , J. Michael Wells , Catherina L Chang , Mark Holmes , Aishath Fazleen , Mark O'Carroll , Ulrike Lorch , Jan Stolk , Amir Majid , Reem Alluhibi , Nicolas Currier , Katy Hayes , Beatrice Chiang , Gary Liu , James Maier , Arthur Lo , Karen Cao , Bahru Habtemariam , Priya S Chockalingam , John J Ko , Sunita Goyal , Amy Simon , Alice Turner