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BIOMARIN R & D Day 2021 Research & Early Development BMN270 : valoctocogene roxaparvovec BMN111 : vosoritide BMN307 BMN255 BMN331 BMN351 BMN349 DINA - 001 Undisclosed Cardiovascular Undisclosed Cardiovascular Undisclosed Cardiovascular Undisclosed Cardiovascular Undisclosed Cardiovascular Undisclosed Cardiovascular Undisclosed CNS Undisclosed CNS Undisclosed CNS Undisclosed CNS Undisclosed CNS Undisclosed CNS Undisclosed CNS Undisclosed CNS Undisclosed CNS Undisclosed CNS Undisclosed Heme & Metab Undisclosed Heme & Metab Undisclosed Heme & Metab Undisclosed Musculoskeletal Undisclosed Musculoskeletal Undisclosed Musculoskeletal Undisclosed Musculoskeletal Undisclosed Musculoskeletal IND - Enabling Phase 1 Phase 2 Phase 3 BIOMARIN R & D Day 2021 R Under Review 1